Asset ↔ target map
advancedactivestalledshared target
Investigator load
- A. PetrovFXN Frataxin Restoration Program, Microdystrophin Gene Transfer, SOD1 Stabilizer3
- D. WhitfieldGBA1 Gene Therapy for Parkinson Disease, SOD1 Antisense Oligonucleotide, SOD1 Stabilizer3
- R. HalvorsenSCN1A Upregulation for Dravet Syndrome, SMN2 Splicing Enhancer, SOD1 Antisense Oligonucleotide3
- E. OkaforJAG1 Modulator for Alagille Syndrome, MECP2 Dosage-Controlled Gene Therapy2
- L. BrandtJAG1 Modulator for Alagille Syndrome, MECP2 Dosage-Controlled Gene Therapy2
- M. CastellanoAnti-Amyloid Monoclonal, CFTR Corrector Triple Combination2
- S. NakamuraHTT-Lowering ASO for Huntington Disease, SCN1A Upregulation for Dravet Syndrome2
- J. MwangiMicrodystrophin Gene Transfer1
- P. AdeyemiCFTR Corrector Triple Combination1
Institution clustering
| Institution | Assets | Advanced |
|---|
| Greenfield Institute for Rare Disease | 3 | 1 |
| Lakeshore Neuroscience Institute | 3 | 2 |
| Capitol Movement Disorders Center | 2 | 1 |
| Riverside Children's Research Center | 2 | 0 |
| Summit Pulmonary Research Group | 2 | 2 |
Relationships are computed from the org's own structured records. Click an asset in the map legend area or visit the portfolio to open a dossier.